Cracking the code on sickle cell treatment just hit the jackpot. A crew of experts gave the nod on Tuesday, giving the green light to a treatment that could be a total game-changer. It's like the golden ticket for a cure that might just rescue more than 100,000 Americans stuck in the clutches of this relentless disease. CRISPR Sickle Cell Cure Deemed Safe: Panel Informs FDA for Patient Use This treatment, brought to you by the genius minds at Vertex Pharmaceuticals and CRISPR Therapeutics, goes by the snazzy name exa-cel. It's not just good; it's a potential trailblazer, set to become the first-ever medicine to use the CRISPR gene-editing magic to tackle a genetic disease head-on. Imagine this: if the FDA gives it the thumbs up, exa-cel could usher in a new era, throwing a lifeline to those stuck in the sickle cell struggle. Fast forward to December 20th, and the FDA is gearing up to decide on another potential game-changer, a gene therapy by Bluebird Bio. The plot thicke
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